Access new resources for advanced therapy development, from candidate identification through market authorization.


This whitepaper explores the transformative impact of Cell and Gene Therapy (CAGT) products in healthcare, focusing on their role in treating previously untreatable conditions and offering hope to patients, particularly those with rare diseases. It discusses the concept of personalized medicine, the involvement of expert patients, the significance of patient-reported outcomes in clinical trials, and the use of digital tools for improved communication and future drug development. Lastly, it also provides an overview of cell therapy and gene therapy and their collective umbrella term, CAGT.
Access new resources for advanced therapy development, from candidate identification through market authorization.
Specialized expertise and customized solutions across 14 therapeutic centers of excellence, including oncology, GI/NASH, pediatrics, neurology and rare diseases.